October 26, 2018Six Month Results of the Phase I Study to Evaluate Safety & Tolerability of RGX-314 Gene Therapy in nAMD SubjectsJeffrey Heier, MD – Ophthalmic Consultants of Boston
May 15, 2018AAV8-antiVEGFfab Ocular Gene Transfer for Neovascular Age-Related MacularDegenerationREGENXBIO
January 12, 2018Adeno-Associated Virus Serotype 8 Gene Therapy Leads to Significant Lowering of Plasma Cholesterol Levels in Humanized Mouse Models of Homozygous and Heterozygous Familial HypercholesterolemiaREGENXBIO
March 12, 2017Non-Clinical Study Examining AAV8.TBG.hLDLR Vector-Associated Toxicity in Chow-Fed Wild-Type and LDLR+/- Rhesus Macaques.REGENXBIO
March 12, 2017Nonclinical Pharmacology/Toxicology Study of AAV8.TBG.mLDLR and AAV8.TBG.hLDLR in a Mouse Model of Homozygous Familial HypercholesterolemiaREGENXBIO
August 10, 2016Delivery of an adeno-associated virus vector into CSF attenuates central nervous system disease in mucopolysaccharidosis type II miceREGENXBIO
July 4, 2016Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine modelREGENXBIO
July 16, 2014Intrathecal Gene Therapy Corrects CNS Pathology in a Feline Model of Mucopolysaccharidosis IREGENXBIO
May 5, 2014Intracerebral administration of adeno-associated viral vector serotype rh.10 carrying human SGSH and SUMF1 cDNAs in children with mucopolysaccharidosis type IIIA disease: results of a phase I/II trialREGENXBIO
